In a landmark study, an international consortium led by researchers at Children's Hospital of Philadelphia (CHOP) published the final results of a key clinical trial of the gene therapy CASGEVY (exagamglogene autotemcel) for the treatment of sickle cell disease in patients 12 years and older with recurrent vaso-occlusive crises (VOCs).
Researchers publish final results of key clinical trial for gene therapy for sickle cell disease retrieved 25 April 2024 from https://medicalxpress.com/news/2024-04-publish-results-key-clinical-trial.html
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