$2.8m gene therapy treatment is America's most expensive drug ever
, with the average US patient suffering from the condition dying at age 37. Bluebird estimates between 1,300 and 1,500 people in the US suffer from the disease.
by adding functional, modified copies of the gene that causes TDBT to a patient's blood, a process that Bluebird calls"one time," but said can still take months to administer.The most expensive drug ever, another gene therapy product called Zolgensma priced at $2.1 million., just like other medicines can benefit from some AI., discovering a way to improve on a gene therapy treatment for Duchenne muscular dystrophy .
The MIT experimenters say a new peptide discovered with the aid of machine learning boosted delivery of DMD drugs 50 fold.
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